Current Clinical Trials
Current Clinical Trials
Also see Published Research Articles for additional publications on Pachyonychia Congenita research and clinical trials.
Completed Clinical Trials
Topical Sirolimus Phase 1b Clinical Trial has been posted at the U.S. National Institutes of Health Clinical Trials.gov site.
First-in-human Mutation-targeted siRNA Phase 1b Trial of an Inherited Skin Disorder
(Molecular Therapy 24 Nov 2009)